Following this puts new work involving it at the top of your briefing, with a note saying why it is there. Links are taken from the source record, never inferred.
This is a narrative review synthesizing recent advances in HSCT and gene-modified stem cell transplantation for sickle cell disease, offering expert perspective on current clinical benchmarks and emerging approaches rather than reporting new primary evidence.
This is a critical appraisal and conceptual review that identifies fundamental gaps between detection and therapeutic capabilities; it raises research questions rather than reporting empirical results from clinical or adequate animal studies.
The Journal of Clinical Endocrinology & Metabolism
Large descriptive cohort establishing clinical phenotype and proposing a novel diagnostic scoring system, but lacking a control group, prospective validation of the score, or powered comparison of outcomes.
A narrative review synthesizing evidence and recommendations on integrating molecular techniques into ART in Africa, addressing policy, infrastructure, and implementation rather than reporting original trial data.