Drug or technology

Gene Therapy

3 developments in the corpus

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AUG 24, 2026 · JOURNAL ARTICLE

Advanced therapy medicinal products in Saudi Arabia: Regulation and development.

Regenerative Therapy

A narrative review synthesizing regulatory frameworks, guidelines, and implementation status of ATMPs in an emerging market; informs policy and institutional strategy rather than clinical practice or mechanistic evidence.

Expert GuidanceMaram Almohaywi Alya Aldahash Advanced Therapy Medicinal Products (atmps)

Reported

Number of ATMPs approved8

Review period2010 to 2025

AUG 19, 2026 · JOURNAL ARTICLE

Targeted Nanoparticle Delivery CRISPR/Cas9: overcoming biological barriers, enhancing stability, and improving therapeutic precision.

International Journal of Pharmaceutics: X

This is a narrative review proposing conceptual frameworks for nanoparticle-mediated CRISPR delivery; it does not report primary experimental data, efficacy outcomes, or comparative evidence.

Hypothesis-GeneratingStimuli-responsive Nanoparticle Crispr/cas9 Sabreena Safuan

Study details

DesignNarrative review

JUN 15, 2026 · REVIEW/PERSPECTIVE

Therapeutic frontiers in ALS: iPSC-based drug discovery, cell therapy, and gene therapy-Advances through 2026.

Regenerative Therapy

Narrative review synthesizing therapeutic developments across multiple ALS modalities without original comparative efficacy data.

Expert GuidanceCell Therapy Shinichi Takahashi Hideyuki Okano

Reported

Proportion of sporadic ALS casesapproximately 90%