OCT 8, 2026 · JOURNAL ARTICLE
BEST-03 | CRISPR-CAS9 CORRECTION IN SEVERE HEMOPHILIA A
Bleeding Thrombosis and Vascular Biology
Background and Aims. Haemophilia A (HA) is a rare X-linked recessive bleeding disorder caused by variants in the F8 gene, which encodes coagulation factor VIII (FVIII). HA is chara